Precision Medicine for Patients & Families
A Personalized Path to Treatment
RareLabs partners with patients and families to build individualized drug discovery programs — transforming a diagnosis into a scientific strategy with real therapeutic potential for rare genetic diseases.
About RareLabs
The Rare Genetic Disease Lab Focused on Treatments
At RareLabs, a division of AlphaRose Therapeutics, we believe every patient and family facing a rare disease deserves a dedicated scientific team working toward a treatment. Our structured, three-step approach moves from patient-derived cell models to multi-modality drug discovery — giving patients and their families a clear roadmap from day one.
Built by a team of scientists, biotech professionals, and parents, we work around the clock to provide answers and solutions. Time is life — and we treat every program with the urgency it deserves.
How We Work
Our Many-Step Approach
Every program is tailored — we assess all available modalities and recommend the best path forward for each patient.
Build the Patient Toolbox
Within 4 weeks, we deliver a personalized Modality Assessment Amenability Plan tailored to each patient — the drug discovery strategy our science team proposes toward a treatment.
- Patient-derived iPSC creation
- CRISPR-corrected controls
- Karyotyping quality assurance
Multi-Modality Drug Discovery
We pursue multiple therapeutic avenues simultaneously to maximize the chance of finding a treatment. Each modality is assessed and tailored to the specific mutation.
- Small molecule screening
- Antisense oligonucleotide (ASO)
- Gene replacement therapy
Keeping You Informed
We keep patients and families updated with clear, easy-to-understand progress reports at every milestone, translating complex science into actionable information.
- Plain-language progress updates
- Milestone-by-milestone reporting
- Direct access to your science team
Therapeutic Modalities
Many Paths to Treatment
We assess all available modalities and recommend the best path forward for each patient's specific condition.
Small Molecule Screening
High-throughput screening of 3,000+ FDA-approved compounds using patient-derived cells to identify potential treatments quickly.
ASO Therapy
Precision antisense oligonucleotides designed to correct gene expression at the RNA level — reversible and highly tunable.
Gene Replacement Therapy
Delivering a functional gene copy to restore normal cellular function, offering potential for long-term, lasting benefit.
Combination Approaches
Integrating multiple therapeutic modalities in parallel to maximize the chance of finding an effective treatment strategy.
Patient & Family First
We work directly with you, keeping patients and families involved and informed at every step.
Speed & Precision
Personalized strategy in 4 weeks with parallel therapeutic approaches to save precious time.
Quality Assured
Rigorous karyotyping and validation at every stage ensures safety and reliability.
Dedicated Team
Scientists and clinicians focused solely on each patient's personalized program.
"Every patient and family facing a rare disease deserves a dedicated scientific team and a clear path forward. That's exactly what we build."
Contact us today to learn how RareLabs can create a personalized drug discovery program for each patient.
Get In Touch
Contact Us
Ready to explore a personalized drug discovery program? We'd love to hear from you.
Let's Start a Conversation
Whether you're a family seeking answers, a foundation exploring partnerships, or a researcher interested in collaboration — we're here to help.